Drug Development News Recent PostsOrphalan Touts First FDA-Approved Wilson’s Disease Treatment Since 1970May 23, 2022IDEAYA Biosciences Receives Orphan Drug Designation for Darovasertib, a PKC Inhibitor, for the Treatment of Uveal MelanomaMay 20, 2022Rare Disease Highlight: Charcot-Marie-Tooth DiseaseMay 19, 2022SQZ Biotechnologies Receives FDA Fast Track Designation for its Lead Cell Therapy Candidate for the Treatment of HPV16+ TumorsMay 18, 2022Allogene Therapeutics Receives FDA Orphan-Drug Designation for ALLO-605, its First TurboCAR™ T Cell Product Candidate, for the Treatment of Multiple MyelomaMay 16, 2022 Archives Archives Select Month May 2022 April 2022 March 2022 February 2022 January 2022 December 2021 November 2021 October 2021 September 2021 August 2021 July 2021 June 2021 May 2021 April 2021 March 2021 February 2021 February 2020 August 2019 July 2019 May 2019 February 2019 June 2018 January 2018 December 2017 February 2017 December 2016 CategoriesCategories Select Category BPG Blog Drug Discovery News Rare Disease Highlight Rare Disease News Regulatory News Uncategorized